Amicus Therapeutics: Managing Orphan and Rare Diseases in the Society

There are 39 categories of diseases in the world. Out of these diseases, we have the rare and orphan diseases. Orphan and rare disease are generally diseases that affect less than 200,000 people in every country. Companies like Amicus Therapeutics, specialize in advanced therapies to treat rare and orphan diseases. Amicus Therapeutics was founded in 2002 but went public in 2007(MarketWatch). The company has 201 to 500 employees, with its headquarters being in Cranbury, New Jersey.



The company uses Chaperone-Advanced Replacement Therapy in developing its products (GoogleNews). They are the producers of Migalastat, a medicine that treats people with Fabry disease. This company generally concentrates on enzyme replacement therapies development. The success of Amicus Therapeutics has placed it at the forefront of the pharmaceutical industry. It has received recognition in having the biggest portfolio of small molecule pharmacological chaperones.


The orphan diseases Amicus Therapeutics deals with include; Genetic Connective Skin Disorder Epidermolysis Bullosa, Lysosomal Storage Disorders Fabry Disease, and Pompe Disease. Amicus Therapeutics seeks to help the lives of afflicted individuals by providing them with accessible medical care. The company takes great pride in their biologics program ATB200/AT2221.


Patients’ Reviews

A lot of people have benefited from the work Amicus Therapeutics is doing. Many of the patients treated for these orphan diseases have testified to how their health improved after embarking on the orphan medicine created by Amicus. The company is able to touch the lives of these people not only through their medicine but also through clinical programs and commercial organization.


The company continues to grow under the management of its CEO John Crowley. Crowley can empathize with a lot of these patients because he has a daughter who suffers from Pompe disease. The company has also expanded by launching Galafold in the European Union. Amicus Therapeutics has also been listed in the ten best companies where investors can buy their stocks.


Amicus Therapeutics has helped save the lives of people with rare diseases, which are barely recognized in the society. Through their continued scientific innovation, they continue to give individuals around the world some hope.

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Oesteo Relief Institute in New Jersey: The right Place to get Treatment for Osteoarthritis

Summary of Osteoarthritis Management

Arthritis is a general term used to describe joint disease or pain. Arthritis comes in more than 100 different forms. More than 50 million people in the US especially women are affected by Arthritis. It is the main cause of disability nationwide.

Osteoarthritis is the most common type of arthritis characterized by the breakdown and wears away of the cartilage, and hence bones begin to rub against each other causing swelling, stiffness and pain. Over time joints becomes weak and pain increases.

Osteoarthritis is a chronic disease, which is incurable and degenerative. Its risk factors include family history, age, previous injury and excess weight. Patients adopting a daily routine, exercise and seeking medical treatment can manage the disease.

Some of the best practices the patient can take for daily routine include gentle exercise before and after bed, adjust sitting position, avoid repetitive movements, control weight and avoid smoking as well as limit themselves to activities within their ability level.

Some of the exercise the patient can do include walking every day to reduce pain and loss of mobility, adopt activities that build muscles. Those activities should be light exercises to help control weight. Activities such as running and jumping that affect your joint should be avoided.

Arthritis can be treated with different kinds of medication. It is necessary to talk to your doctor to see which medication that works best for you. Look for a qualified Physical Therapy expert to help you manage to reduce pain and mobility loss. If the conservative methods fail, a patient can adopt for surgery. Orthopedic Specialists can explain to you the advantage and limitation of each option. Investing in the right health care and self-management tool can guarantee a long, high-quality life.

Osteo Relief Institute in New Jersey

Number one priority in today’s health environment is getting the right doctor to trust. Osteo Relief Institute in New Jersey is a multidisciplinary clinic that treats patients as a family. Their main aim is to ensure patients avoid surgery as well as provide them with safe and effective medical treatments. Staffs at Osteo Relief Institute are well trained to attend to patients professionally.

Osteo Relief Institute uses the state of the art technology to help identify the patient pain and provide the right medical treatment to treat osteoarthritis. No introductory screening fee is charged to determine the right treatment method for the patient.

Osteo Relief Institute is dedicated to ensuring you stay healthy, active and live a long life without discomfort. They have a pain relief program of the knee, which frequently results in great success with promising outcomes to the patient.

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